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Beatriz Campo Fernandez
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Journal Articles

Ex Vivo Lentiviral Hematopoietic Stem Cell (HSC) Gene Therapy May Represent a Curative Therapy for the Life-Threatening Inborn Error of Immunity Severe Combined Immunodeficiency Due to Adenosine Deaminase (ADA) Deficiency (ADA-SCID)

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Katelyn Masiuk, Jinhua Xu-Bayford, Augustine Fernandes, Konstantinos Vazouras, Danilo Pellin, Havinder Hara, Sohini Roy, Beatriz Campo Fernandez, Thao Thai Dang, Kimberly Gilmour, Elena Alvarez Mediavilla, Beatrice Curio-Penny, Gráinne O'Toole, Rima Ahmed, Jordyn Arnold, Elizabeth Garabedian, Harry L Malech, Kenneth Cornetta, Claire Booth, Donald B. Kohn
Journal: Blood
Blood (2024) 144 (Supplement 1): 1051.
https://doi.org/10.1182/blood-2024-202543
Published: 2024
Journal Articles

Α-Globin Lentiviral Vectors for Hematopoietic Stem Cell Gene Therapy of α-Thalassemia

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Eva Segura, Kevin Tam, Beatriz Campo Fernandez, Tippi C. MacKenzie, Roger Hollis, Donald B. Kohn
Journal: Blood
Blood (2023) 142 (Supplement 1): 7131.
https://doi.org/10.1182/blood-2023-190619
Published: 2023
Journal Articles

Base Editing of Hematopoietic Stem Cells Rescues T-Cell Development for CD3d Severe Combined Immunodeficiency

Free
Grace McAuley, Gloria Yiu, Gregory A. Newby, Beatriz Campo Fernandez, Xiaomeng Wu, Patrick Chang, Kelcee Everette, Zulema Romero Garcia, David R. Liu, Gay M. Crooks, Donald B. Kohn
Journal: Blood
Blood (2022) 140 (Supplement 1): 1641–1642.
https://doi.org/10.1182/blood-2022-170634
Published: 2022
Journal Articles

Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency

Free
Clinical Trials & Observations
Bryanna Reinhardt, Omar Habib, Kit L. Shaw, Elizabeth Garabedian, Denise A. Carbonaro-Sarracino, Dayna Terrazas, Beatriz Campo Fernandez, Satiro De Oliveira, Theodore B. Moore, Alan K. Ikeda, Barbara C. Engel, Gregory M. Podsakoff, Roger P. Hollis, Augustine Fernandes, Connie Jackson, Sally Shupien, Suparna Mishra, Alejandra Davila, Jack Mottahedeh, Andrej Vitomirov, Wenzhao Meng, Aaron M. Rosenfeld, Aoife M. Roche, Pascha Hokama, Shantan Reddy, John Everett, Xiaoyan Wang, Eline T. Luning Prak, Kenneth Cornetta, Michael S. Hershfield, Robert Sokolic, Suk See De Ravin, Harry L. Malech, Frederic D. Bushman, Fabio Candotti, Donald B. Kohn
Journal: Blood
Blood (2021) 138 (15): 1304–1316.
https://doi.org/10.1182/blood.2020010260
Published: 2021
Includes: Supplemental data
Journal Articles

Lentiviral Gene Therapy with Autologous Hematopoietic Stem and Progenitor Cells (HSPCs) for the Treatment of Severe Combined Immune Deficiency Due to Adenosine Deaminase Deficiency (ADA-SCID): Results in an Expanded Cohort

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Donald B. Kohn, MD, Kit L. Shaw, PhD, Elizabeth Garabedian, RN, MS, Denise Ann Carbonaro-Sarracino, PhD, Theodore B. Moore, MD, Satiro N. De Oliveira, MD, Gay M. Crooks, MD, John Tse, Sally Shupien, Dayna Terrazas, Alejandra Davila, Amalia Icreverzi, PhD, Allen Yu, Krista M. Chun, Christian E. Casas, Provaboti Barman, PhD, Maritess Coronel, Beatriz Campo Fernandez, PhD, Ruixue Zhang, Roger P. Hollis, PhD, Chilenwa Uzowuru, Hilory Ricketts, Jinhua Xu Bayford, Valentina Trevisan, Serena Arduini, PhD, Frances Lynn, Mahesh Kudari, MBBS, MA, Andrea Spezzi, MD MBBS, Lilith Reeves, MS, MT(ASCP), Kenneth Cornetta, Robert A. Sokolic, MD, Roberta Parrott, BS, Rebecca Buckley, MD, Claire Booth, Fabio Candotti, MD, Harry L. Malech, MD, Adrian J. Thrasher, MBBS, PhD FMedSci, H. Bobby Gaspar, MBBS, PhD
Journal: Blood
Blood (2019) 134 (Supplement_1): 3345.
https://doi.org/10.1182/blood-2019-123432
Published: 2019