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    Alexandra Laura Miller
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    Journal Articles

    Longer Term Follow-up on the First Patients with Severe Hemoglobinopathies Treated with Lentiglobin Gene Therapy

    Free
    Marina Cavazzana, MD PhD, Salima Hacein-Bey-Abina, Pharm.D.,PhD, Emmanuel Payen, Elisa Magrin, PhD, Alessandra Magnani, MD PhD, Michaela Semeraro, Laure Caccavelli, Fabien Touzot, MD PhD, Francois Lefrere, Sr., Felipe Suarez, MDPhD, Olivier Hermine, Valentine Brousse, MD, Catherine Poirot, Despina Moshous, Philippe Bourget, PhD, Wassim El Nemer, PhD, Pablo Bartolucci, MD PhD, Leslie Weber, Herve Puy, MD, Jean-François Meritet, David Grévent, MD, Yves Beuzard, MD, Stany Chretien, Thibaud Lefebvre, Mohammed Asmal, MD PhD, Alexandra Laura Miller, Mariane De Montalembert, MD PhD, Stephane Blanche, MD, Philippe Leboulch, MD, Jean-Antoine Ribeil, MD
    Journal: Blood
    Blood (2017) 130 (Supplement 1): 4609.
    https://doi.org/10.1182/blood.V130.Suppl_1.4609.4609
    Published: 2017

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