Patient characteristics
No. of patients enrolled | 100 |
| Median patient sex, M/F | 67/33 |
| Median patient age at diagnosis, y (range) | 1.4 (0.1-14) |
| Median patient age at HSCT, y (range) | 2.5 (0.3-15) |
| Median interval between diagnosis and HSCT, mo (range) | 6 (0.3-49) |
| Median WBC count at diagnosis,* × 109/L (range) | 34 (3-240) |
| Median monocyte count at diagnosis,† × 109/L (range) | 5.5 (1-50) |
| Median platelet count at diagnosis,‡ × 109/L (range) | 65 (9-530) |
| Percentage of HbF at diagnosis§ (range) | 9 (0-80) |
| Karyotype | |
| Normal karyotype | 66 |
| Monosomy 7 | 20 |
| Trisomy 8 | 9 |
| Other abnormalities | 4 |
| Missing/unknown | 1 |
| No. of patients with clinical evidence of NF1∥ | 14 |
| Median WBC count at HSCT,¶ × 109/L (range) | 9.6 (0.7-320) |
| Percentage of marrow blasts at HSCT** (range) | 6 (0-85) |
| Splenectomy before HSCT | 24 |
| Median spleen size at HSCT,†† cm (range) | 5 (0-16) |
| Patient HCMV serology | |
| Negative | 57 |
| Positive | 39 |
| Unknown | 4 |
No. of patients enrolled | 100 |
| Median patient sex, M/F | 67/33 |
| Median patient age at diagnosis, y (range) | 1.4 (0.1-14) |
| Median patient age at HSCT, y (range) | 2.5 (0.3-15) |
| Median interval between diagnosis and HSCT, mo (range) | 6 (0.3-49) |
| Median WBC count at diagnosis,* × 109/L (range) | 34 (3-240) |
| Median monocyte count at diagnosis,† × 109/L (range) | 5.5 (1-50) |
| Median platelet count at diagnosis,‡ × 109/L (range) | 65 (9-530) |
| Percentage of HbF at diagnosis§ (range) | 9 (0-80) |
| Karyotype | |
| Normal karyotype | 66 |
| Monosomy 7 | 20 |
| Trisomy 8 | 9 |
| Other abnormalities | 4 |
| Missing/unknown | 1 |
| No. of patients with clinical evidence of NF1∥ | 14 |
| Median WBC count at HSCT,¶ × 109/L (range) | 9.6 (0.7-320) |
| Percentage of marrow blasts at HSCT** (range) | 6 (0-85) |
| Splenectomy before HSCT | 24 |
| Median spleen size at HSCT,†† cm (range) | 5 (0-16) |
| Patient HCMV serology | |
| Negative | 57 |
| Positive | 39 |
| Unknown | 4 |
WBC indicates white blood cell.
*Three unknown; †6 unknown; ‡3 unknown; §23 unknown; ∥8 unknown; ¶8 unknown; **13 unknown; ††6 unknown.