Expression of Human F.IX in CD-1 Mice After Intravenous Injection of AAV-CMV-F.IX at Day 1 of Life
Days Postinjection . | Expression of hF.IX in Plasma (ng/mL)-150 . | % Hepatocytes Expressing hF.IX-151 . |
---|---|---|
5 | 77 (±24) | 3 (±0.6) |
14 | 15 (±6) | 1.3 (±0.5) |
35 | 2 (±3.5) | ND |
60 | 0 | ND |
240-300 | 0 | 0.25 (±0.1) |
Days Postinjection . | Expression of hF.IX in Plasma (ng/mL)-150 . | % Hepatocytes Expressing hF.IX-151 . |
---|---|---|
5 | 77 (±24) | 3 (±0.6) |
14 | 15 (±6) | 1.3 (±0.5) |
35 | 2 (±3.5) | ND |
60 | 0 | ND |
240-300 | 0 | 0.25 (±0.1) |